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  • Simantini Singh Deo

Agios’ PYRUKYND® (mitapivat) Receives Positive CHMP Opinion For Treatment Of Adults With Thalassemia
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Kiniksa Pharmaceuticals Receives U.S. Orphan Drug Designation For KPL-387 To Treat Pericarditis

Simantini Singh Deo

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Agios’ PYRUKYND® (mitapivat) Receives Positive CHMP Opinion For Treatment Of Adults With Thalassemia

CHMP gives positive opinion for Agios’ PYRUKYND to treat alpha- and beta-thalassemia in adults.

Simantini Singh Deo

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Kiniksa Pharmaceuticals Receives U.S. Orphan Drug Designation For KPL-387 To Treat Pericarditis

FDA grants Orphan Drug Designation to Kiniksa’s KPL-387 for treating pericarditis, supporting rare disease innovation.

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Prelude Therapeutics Welcomes Katina Dorton, J.D., MBA, To Its Board of Directors

Prelude Therapeutics appoints Katina Dorton to its Board, enhancing precision oncology leadership and strategic expertise.

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Achieve Life Sciences Secures FDA Commissioner’s Priority Voucher For Cytisinicline To Support Nicotine Cessation In Vaping And E-Cigarette Users

Achieve Life Sciences receives FDA priority voucher for cytisinicline, advancing first e-cigarette cessation therapy.

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