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Simantini Singh Deo
CHMP gives positive opinion for Agios’ PYRUKYND to treat alpha- and beta-thalassemia in adults.
Simantini Singh Deo
FDA grants Orphan Drug Designation to Kiniksa’s KPL-387 for treating pericarditis, supporting rare disease innovation.
Simantini Singh Deo
Prelude Therapeutics appoints Katina Dorton to its Board, enhancing precision oncology leadership and strategic expertise.
Simantini Singh Deo
Achieve Life Sciences receives FDA priority voucher for cytisinicline, advancing first e-cigarette cessation therapy.
Simantini Singh Deo